Канал: Friedreich's Ataxia Research Alliance

Lexeo Therapeutics LX2006 Cardiac Gene Therapy for Friedreich's Ataxia Informational Webinar

Lexeo Therapeutics LX2006 Cardiac Gene Therapy for Friedreich's Ataxia Informational Webinar

Astellas Pharma ASP2016 Cardiac Gene Therapy for Friedreich's Ataxia Informational Webinar

Astellas Pharma ASP2016 Cardiac Gene Therapy for Friedreich's Ataxia Informational Webinar

FA Community Conversations Genetic Therapies Webinar | Recorded August 29, 2024

FA Community Conversations Genetic Therapies Webinar | Recorded August 29, 2024

FARA Flash Talks 2024 Series — Session 2

FARA Flash Talks 2024 Series — Session 2

FARA Flash Talks 2024 Series — Session 1

FARA Flash Talks 2024 Series — Session 1

FA Community Conversations | May 2, 2024

FA Community Conversations | May 2, 2024

Applying for CDMRP/PRMRP Grants Training | April 25, 2024

Applying for CDMRP/PRMRP Grants Training | April 25, 2024

FARA Pediatric Research Initiatives Webinar | January 25, 2024

FARA Pediatric Research Initiatives Webinar | January 25, 2024

FARA Wrapped 2023

FARA Wrapped 2023

Living with FA & Contributing to Research – The Impact of Two Sisters: Meet Scarlett & Lilah

Living with FA & Contributing to Research – The Impact of Two Sisters: Meet Scarlett & Lilah

FA Community: We're Just Getting Started

FA Community: We're Just Getting Started

FA Symposium 2023: Mental Wellness Workshop

FA Symposium 2023: Mental Wellness Workshop

FA Symposium 2023: Gene Therapy Panel–The Patient Experience in Rare Diseases (Part 7 of 7)

FA Symposium 2023: Gene Therapy Panel–The Patient Experience in Rare Diseases (Part 7 of 7)

FA Symposium 2023: A Strategy for Funding Friedreich's Ataxia Research (Part 6 of 7)

FA Symposium 2023: A Strategy for Funding Friedreich's Ataxia Research (Part 6 of 7)

FA Symposium 2023: Rare Disease Prescription Roadmap (Part 5 of 7)

FA Symposium 2023: Rare Disease Prescription Roadmap (Part 5 of 7)

FA Symposium 2023: Living with Friedreich's Ataxia (Part 4 of 7)

FA Symposium 2023: Living with Friedreich's Ataxia (Part 4 of 7)

FA Symposium 2023: Friedreich's Ataxia Treatment Pipeline–Clinical Stage Programs (Part 3 of 7)

FA Symposium 2023: Friedreich's Ataxia Treatment Pipeline–Clinical Stage Programs (Part 3 of 7)

FA Symposium 2023: Clinical Management of Friedreich's Ataxia (Part 2 of 7)

FA Symposium 2023: Clinical Management of Friedreich's Ataxia (Part 2 of 7)

FA Symposium 2023: Welcome to the 2023 Friedreich's Ataxia Symposium (Part 1 of 7)

FA Symposium 2023: Welcome to the 2023 Friedreich's Ataxia Symposium (Part 1 of 7)

FARA Flash Talks 2023 Series - Session 4

FARA Flash Talks 2023 Series - Session 4

FARA Flash Talks 2023 Series - Session 3

FARA Flash Talks 2023 Series - Session 3

FARA Flash Talks 2023 Series - Session 2

FARA Flash Talks 2023 Series - Session 2

FARA Flash Talks 2023 Series - Session 1

FARA Flash Talks 2023 Series - Session 1

2 Minute Mechanisms: omaveloxolone

2 Minute Mechanisms: omaveloxolone

A History of Omav and the FA Community

A History of Omav and the FA Community

Thank You for giving The Gift of Research

Thank You for giving The Gift of Research

Episode 15: 2022 In Review

Episode 15: 2022 In Review

Researcher, Clinical Trial Participant, Ambassador, & Advocate: Meet Shandra

Researcher, Clinical Trial Participant, Ambassador, & Advocate: Meet Shandra

Episode 14: Community Participation in Research

Episode 14: Community Participation in Research

FARA - CHOP Symposium - Sep 24th & 25th - Part 1

FARA - CHOP Symposium - Sep 24th & 25th - Part 1

FARA - CHOP Symposium - Sep 24th and 25th - Part 2

FARA - CHOP Symposium - Sep 24th and 25th - Part 2

FARA - CHOP Symposium - Sep 24th and 25th - Part 3

FARA - CHOP Symposium - Sep 24th and 25th - Part 3

FARA - CHOP Symposium - Sep 24th and 25th - Part 4

FARA - CHOP Symposium - Sep 24th and 25th - Part 4

FARA Informational Webinar with Larimar Therapeutics

FARA Informational Webinar with Larimar Therapeutics

Episode 13: Hand and Arm Function in FA

Episode 13: Hand and Arm Function in FA

2022 FARA Flash Talks Series - Part 4

2022 FARA Flash Talks Series - Part 4

2022 FARA Flash Talk Series - Part 3 - May 19th

2022 FARA Flash Talk Series - Part 3 - May 19th

2022 FARA Flash Talk Series - Part 2 - May 12th

2022 FARA Flash Talk Series - Part 2 - May 12th

Episode 12: Patient Reported Outcomes

Episode 12: Patient Reported Outcomes

2022 FARA Flash Talk Series - Part 1 - May 5th

2022 FARA Flash Talk Series - Part 1 - May 5th

CDMRP PRMRP Informational Webinar - Apr 5, 2022

CDMRP PRMRP Informational Webinar - Apr 5, 2022

Episode 11: Role of Iron in FA

Episode 11: Role of Iron in FA

The Ataxian Movie - Q & A - Mar 3, 2022

The Ataxian Movie - Q & A - Mar 3, 2022

Episode 10: Frataxin Function

Episode 10: Frataxin Function

Episode 9: FARA's Contribution to Advancing Science

Episode 9: FARA's Contribution to Advancing Science

"This is our FAmily": Meet the Juips

"This is our FAmily": Meet the Juips

Episode 8: FACOMS

Episode 8: FACOMS

FARA Energy Ball 2021

FARA Energy Ball 2021

Track FA Webinar - Sept 20, 2021

Track FA Webinar - Sept 20, 2021

2021 rideATAXIA Global Challenge

2021 rideATAXIA Global Challenge

Episode 7: The Balancing Act of Frataxin

Episode 7: The Balancing Act of Frataxin

Episode 6: Track-FA

Episode 6: Track-FA

Episode 5: Gene Therapy

Episode 5: Gene Therapy

Understanding the Inheritance of FA

Understanding the Inheritance of FA

Understanding the Genetics of Friedreich's Ataxia

Understanding the Genetics of Friedreich's Ataxia

Gene Therapy for Friedreich's Ataxia

Gene Therapy for Friedreich's Ataxia

Episode 4: FXN Gene Silencing

Episode 4: FXN Gene Silencing

Episode 3: Drug Targets in the Central Nervous System

Episode 3: Drug Targets in the Central Nervous System

Episode 2: Sensory Neurons

Episode 2: Sensory Neurons

How to Register for a rideATAXIA Event on Mobile

How to Register for a rideATAXIA Event on Mobile

FARA Call To Action Jan 5, 2021

FARA Call To Action Jan 5, 2021

FARA End of Year Vid 2020

FARA End of Year Vid 2020

rideATAXIA Year in Review 2020

rideATAXIA Year in Review 2020

Episode 1: iPSC bank

Episode 1: iPSC bank

Minutes of Science Intro: FARA Garden

Minutes of Science Intro: FARA Garden

FARA Energy Ball 2020 - Thank You For Your Support

FARA Energy Ball 2020 - Thank You For Your Support

2020 FARA Energy Ball

2020 FARA Energy Ball

Welcome to the Broad Institute!

Welcome to the Broad Institute!

Tour of the Lab at University of Florida

Tour of the Lab at University of Florida

Tour of USFH Ataxia Research Center

Tour of USFH Ataxia Research Center

Tour of the lab at St Jude with Dr. Aseem Ansari!

Tour of the lab at St Jude with Dr. Aseem Ansari!

Tour of University of Alabama with Drs. Marek and Jill Napierala!

Tour of University of Alabama with Drs. Marek and Jill Napierala!

Tour of the lab at University of Oklahoma with Dr. Sanjay Bidichandani!

Tour of the lab at University of Oklahoma with Dr. Sanjay Bidichandani!

Tour of UCLA with Dr. Perlman

Tour of UCLA with Dr. Perlman

Meet Dr. Javier Santos’ team at Universidad de Buenos Aires!

Meet Dr. Javier Santos’ team at Universidad de Buenos Aires!

Amalia Introduces Us to the Team at Ataxia de Friedreich do Brasil

Amalia Introduces Us to the Team at Ataxia de Friedreich do Brasil

Interview with Christian Rummey, Clinical Data Science Gmbh

Interview with Christian Rummey, Clinical Data Science Gmbh

Visit Dr. Mirella Dottori at the University of Wollongong

Visit Dr. Mirella Dottori at the University of Wollongong

Tour of Murdoch Children’s Research Institute with Dr. Louise Corben

Tour of Murdoch Children’s Research Institute with Dr. Louise Corben

Tour of Università degli Studi di Roma "Tor Vergata" with Dr. Aquilino

Tour of Università degli Studi di Roma "Tor Vergata" with Dr. Aquilino

Get to Know the Friedreich Ataxia Lebanese Association (FALA)

Get to Know the Friedreich Ataxia Lebanese Association (FALA)

Tour of Hélène Puccio's lab at IGBMC

Tour of Hélène Puccio's lab at IGBMC

Tour of Hélène Puccio's lab at the Institute NeuroMyoGène

Tour of Hélène Puccio's lab at the Institute NeuroMyoGène

Interview with Dr. Hélène Puccio of IGBMC

Interview with Dr. Hélène Puccio of IGBMC

Tour of University of California San Diego with Dr. Stephanie Cherqui

Tour of University of California San Diego with Dr. Stephanie Cherqui

Interview with Dr. Pandolfo of the Universite Libre de Bruxelles

Interview with Dr. Pandolfo of the Universite Libre de Bruxelles

FARA Ireland Activities

FARA Ireland Activities

CHUM, Montreal. Dr. DUQUETTE

CHUM, Montreal. Dr. DUQUETTE

CHOP Dr Wilson

CHOP Dr Wilson

CHOP, Lynch Interview

CHOP, Lynch Interview

Global Challenge Pilot Intro

Global Challenge Pilot Intro

Welcome to the rideATAXIA Virtual Challenge!

Welcome to the rideATAXIA Virtual Challenge!

AFAF's Battle Cry

AFAF's Battle Cry

rideATAXIA Global Challenge 2020

rideATAXIA Global Challenge 2020

Friedreich's ataxia (FA) Global Patient Registry Tutorial

Friedreich's ataxia (FA) Global Patient Registry Tutorial

Get Us Together, It's Never Been Done Before

Get Us Together, It's Never Been Done Before

Maybe This Won't Take Forever

Maybe This Won't Take Forever

Before There Was a FARA

Before There Was a FARA

Solitude - Living with Friedreich's Ataxia

Solitude - Living with Friedreich's Ataxia

FARA Energy Ball 2018

FARA Energy Ball 2018

ENERGY BALL VIDEO 2017

ENERGY BALL VIDEO 2017

Life With Friedreich's Ataxia - Always Changing

Life With Friedreich's Ataxia - Always Changing

FA Patient Focused Drug Development Meeting

FA Patient Focused Drug Development Meeting

FARA 2016 Thanks

FARA 2016 Thanks

FARA Energy Ball 2016

FARA Energy Ball 2016

FARA Energy Ball 2015

FARA Energy Ball 2015

FARA Energy Ball 2014

FARA Energy Ball 2014

FARA Energy Ball 2013

FARA Energy Ball 2013

Universal Hope by: Jack Dewitt

Universal Hope by: Jack Dewitt

FARA In Game Presentation at the Tampa Bay Lighting Game 2.1.13

FARA In Game Presentation at the Tampa Bay Lighting Game 2.1.13

2012 FARA Energy Ball Video

2012 FARA Energy Ball Video

Ronde Barber and Kyle Bryant talk about Friedreich's Ataxia

Ronde Barber and Kyle Bryant talk about Friedreich's Ataxia

Fara Energy Ball 2011

Fara Energy Ball 2011

The cast of Army Wives - Take Action, Donate, Cure FA.

The cast of Army Wives - Take Action, Donate, Cure FA.

FARA Energy Ball Video 2009

FARA Energy Ball Video 2009

Introduction to Friedreich's Ataxia and FARA

Introduction to Friedreich's Ataxia and FARA