Introduction and Heatmap Overview
Amena Smith Fine, MD, PhD (Kennedy Krieger Institute)

Key Successes and Challenges: Hypomyelination with Brainstem and Spinal cord involvement and Leg spasticity (HBSL)
Amena Smith Fine, MD PhD (Kennedy Krieger Institute)

Key Successes: Leukoencephalopathy with Brainstem and Spinal Cord Involvement and Lactate Elevation (LBSL)
Beth Frigola McGinn (Cure LBSL)

Key Challenges: Leukoencephalopathy with Brainstem and Spinal Cord Involvement and Lactate Elevation (LBSL)
Christina Nemeth Mertz, PhD (Kennedy Krieger Institute)

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