Learn about Arcturus' approach to treating cystic fibrosis (CF). CF is a genetic disease that affects approximately 100,000 people worldwide and over 30,000 people in the US. It's caused by mutations in the cystic fibrosis transmembrane regulator gene (CFTR). Learn how this investigational mRNA therapy targets the root cause of CF by restoring the CFTR protein.
#CysticFibrosis #CF #CFTR #mRNATherapeutics
Ещё видео!