Day 1: General Session, Global Genes' Medical Science Advisory Board, Panel Host: Peter Goodhand Participants: Ryan Taft, Ph.D., Anthony Philippakis, M.D., Ph.D., Alvin Shih, M.D., M.B.A.
New technologies and new scientific understandings are bringing about changes that can truly transform both research and development for treatments and clinical care for rare diseases. How will these affect patients and their families in the next few years? And how can patients and their families participate in this transformation?
