People with cystic fibrosis (CF) can live longer, better-quality lives thanks to new treatments called CFTR modulators. These medications target gene mutations present in CF and can significantly minimize symptoms and reduce complications. When started early, they can even eliminate some of the worst effects of CF. Here, Mai ElMallah, MD, a pediatric pulmonologist at Duke Health, discusses CFTR modulators, how they work, and who can benefit.
00:00 Intro
00:14 What is cystic fibrosis?
00:33 What are CFTR modulators?
01:11 How successful are CFTR modulators?
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