Medical Pioneer: First Patient Receives Unique Rare Disease Therapy Developed At Uc San Diego

Medical Pioneer: First Patient Receives Unique Rare Disease Therapy Developed at UC San Diego

UC San Diego Health

San Diego woman with rare disease receives first breakthrough treatment at UC San Diego

CBS 8 San Diego

Medical Pioneer: first patient receives unique rare disease therapy developed at UC San Diego

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Genetic Alliance UK

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UC San Francisco (UCSF)

Family diagnosed with rare disease works to raise awareness

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CBC News: The National

Ottawa baby pioneers gene therapy for rare disease

UC San Diego researcher gets $15 million for nanosponge therapy

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Cure Rare Disease

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